Natural History Study of Duchenne Muscular Dystrophy
Actively RecruitingObservationalOther Therapeutic Approaches
Study Overview
- Age
- 2–30 years
- Phase
- Observational
- Sponsor
- University Medical Center
- Therapeutic Approach
- Other Therapeutic Approaches
- Variant Requirement
- Genetically confirmed DMD; all mutation types eligible
- Eligible Sex
- Male
- Ambulation
- Ambulatory and Non-Ambulatory
- Countries
- United States
Study Requirements and Criteria
Steroid Use
All steroid use patterns accepted; documented at enrollment
Inclusion Criteria
Male with confirmed DMD aged 2–30 years. Willing to attend annual study visits. Parent or guardian consent for minors.
Exclusion Criteria
Participation in interventional gene therapy trial within 12 months. Inability to attend follow-up visits.
Clinical Trial Registry
NCT ID
NCT02353637This information is provided for educational purposes only. Always consult the study investigators before making medical decisions.